Analysis Shows Rare Diseases Comprise Eighty Percent of Approved Gene Therapies
A registry-based cross-sectional analysis reveals that rare conditions account for eighty percent of approved gene therapy products and forty-four percent ...
A registry-based cross-sectional analysis reveals that rare conditions account for eighty percent of approved gene therapy products and forty-four percent ...
A systematic review of nine studies across West Africa highlights substantial maternal and perinatal risks for pregnant women with sickle ...
Researchers evaluated an interpretable machine-learning model that identified subtle facial morphometric patterns distinguishing pediatric participants with sickle cell disease from ...
Researchers have demonstrated that the non-IMiD small-molecule degrader SH6 reactivates fetal hemoglobin across erythroid cell lines, patient-derived primary cells, and ...
A 2026 review in Eye and Vision outlines current medical and surgical strategies for managing sickle cell retinopathy, emphasizing the ...
A systematic review in Annals of Hematology finds that pyruvate kinase activators improve hemoglobin and reduce transfusion needs in PKD ...
A retrospective cohort study found pediatric patients with sickle cell disease-associated osteonecrosis of the femoral head experienced significantly higher total ...
A pilot study evaluating virtual reality headsets among hospitalized adults with sickle cell disease demonstrated high acceptability, low side effects, ...
The first University of Dodoma scientific conference on health compiled research showing major gains in maternal survival and kidney transplantation ...
A cross-sectional investigation conducted at the University of Benin Teaching Hospital in Benin City, Edo State, Nigeria, has found that ...
© 2026 Scienmag - Science Magazine
© 2026 Scienmag - Science Magazine