Gene Therapy

Scientists uncover the mysteries of how viruses evolveCredit: ETH Zürich / Stephan Tette The team say their findings have implications for the treatment of viruses in future. Researchers from the Universities of York and Leeds,…

Researchers detail another gene target that could be the crucial link to curing different cancersCredit: Chinese Medical Journal Humans have been plagued by a myriad of deadly cancers since ages. Parallelly, they have also been…

An ECI webinar on July 21, 2021 The webinar, which will be held on July 21, will feature a keynote presentation by Greg Russotti followed by interactive panel sessions on the future perspectives for digitized manufacturing and real-time…

Credit: RCSI Scientists have developed polypeptide-based materials that act as effective vectors for delivering gene therapies. The first-of-its-kind platform enables the vectors to be adapted to suit the specific gene therapy cargo.…

A single dose of AAV8-TNAP-D10 may be safe and effective for hypophosphatasiaCredit: Sanford Burnham Prebys LA JOLLA, CALIF. - June 7, 2021 - A preclinical study led by scientists at Sanford Burnham Prebys has established that…

Credit: ETH Zurich Many modern fitness trackers and smartwatches feature integrated LEDs. The green light emitted, whether continuous or pulsed, penetrates the skin and can be used to measure the wearer's heart rate during physical…

Converting a pathogenic hemoglobin gene to a benign variant enables healthy blood cell production in an animal model of sickle cell disease Sickle cell disease (SCD) is the most common deadly genetic disorder, affecting more than 300,000…

Researchers create novel CRISPR-based fly species as a new method of controlling gene drive spreadCredit: Akbari lab, UC San Diego CRISPR-based technologies offer enormous potential to benefit human health and safety, from disease…

NIH- and USU- led study links ALS to a fat manufacturing gene and maps out a genetic therapyCredit: Courtesy of the NIH/NINDS. In a study of 11 medical-mystery patients, an international team of researchers led by scientists at the…

Genetics toolkit targets less researched Culex mosquitoes, which transmit West Nile virus and avian malariaCredit: Gantz Lab, UC San Diego Since the onset of the CRISPR genetic editing revolution, scientists have been working to leverage…

Skokie, IL - The International Society for Stem Cell Research (ISSCR), today released updated guidelines for stem cell research and its translation to medicine. The update reflects emerging advances including, stem cell-based embryo…

MUSC Hollings Cancer Center researchers improve peptide siRNA drug carriers for use as a novel cancer treatmentCredit: MUSC/Marquel Coaxum MUSC Hollings Cancer Center researchers are exploring the use of peptide carriers for the…

Dartmouth researchers are about to bring change to the treatment of pancreatic cancer with a novel biomarker technology that predicts chemotherapy response and potential benefit of epigenetic therapy in patients with pancreatic…

Researchers from IDC Herzliya and Bar-Ilan University develop a novel software tool to quantify potential CRISPR-induced errors CRISPR technology allows researchers to edit genomes by altering DNA sequences and by thus modifying gene…

The first project will explore regenerative cell therapy to treat blood cancers, heart failure and eye degeneration 21 May 2021, Singapore - The SingHealth Duke-NUS Academic Medical Centre (AMC) announced the launch of a research institute…

Base editing is a novel gene editing approach that can precisely change individual building blocks in a DNA sequence. By installing such a point mutation in a specific gene, an international research team led by the University of Zurich…

Grew over $200 billion since 2010, outlines new areas of promising application WASHINGTON, DC (May 19, 2021) - Human genetics and genomics contributed $265 billion to the U.S. economy in 2019 and has the potential to drive significant…

CORVALLIS, Ore. - Researchers at Oregon State University have found a key new piece of the puzzle in the quest to use gene therapy to enable people born deaf to hear. The work centers around a large gene responsible for an inner-ear…

Credit: Griffith University An international team of scientists from the Menzies Health Institute Queensland (MHIQ) at Griffith University and from City of Hope, a research and treatment center for cancer, diabetes and other…

Credit: Plückthun Lab A new technology developed by UZH researchers enables the body to produce therapeutic agents on demand at the exact location where they are needed. The innovation could reduce the side effects of cancer…